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Rare Diseases, Orphan Drugs, and Orphaned Patients
Table 1.
Numbers of Orphan Drugs Approved by the FDA for Orphan Diseases
| Disease | Number Approved |
|---|---|
| Data adapted from Haffner, M. N. Engl. J. Med. ©2006 | |
| Cancers | 38 |
| Metabolic Diseases | 37 |
| Infectious Diseases | 23 |
| Neurological Diseases | 18 |
| Hematological Diseases | 16 |
| Pulmonary Diseases | 9 |
| Poisonings | 9 |
